Sponsor Pipeline

Alnylam Pharmaceuticals Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-08-16
26
Active Trials
20
Recruiting
5
Phase 3
9
Disease Areas
11
Changes, 30 Days
What Changed in the Last 30 Days
DetectedTrialChange
2026-08-15 NCT07052903
TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With…
Trial sites expanded: 240 -> 251 locations
2026-08-15 NCT07223203
TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With…
Trial sites expanded: 41 -> 48 locations
2026-08-13 NCT07636811
A Study to Evaluate Mivelsiran in Adult Participants With Early-Stage Down…
Recruitment opened
2026-08-13 NCT07575308
HMBeacon: A Phase 2 Study to Evaluate ALN-6400 in Adult and Adolescent Female Patients…
Recruitment opened
2026-08-13 NCT07575308
HMBeacon: A Phase 2 Study to Evaluate ALN-6400 in Adult and Adolescent Female Patients…
Trial sites expanded: 1 -> 4 locations
2026-07-24 NCT07465224
A Study to Evaluate ALN-4324 on Insulin Sensitivity in Adults With Type 2 Diabetes…
Enrollment reduced: 40 -> 24 participants
2026-07-24 NCT07223203
TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With…
Trial sites expanded: 29 -> 41 locations
2026-07-24 NCT07052903
TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With…
Enrollment increased: 1250 -> 1750 participants
2026-07-24 NCT07052903
TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With…
Trial sites expanded: 233 -> 240 locations
2026-07-24 NCT06845202
A Study to Evaluate ALN-4324 in Overweight to Obese Healthy Volunteers and in Overweight…
overall status: Recruiting → Active, Not Recruiting
2026-07-24 NCT06845202
A Study to Evaluate ALN-4324 in Overweight to Obese Healthy Volunteers and in Overweight…
Enrollment reduced: 144 -> 105 participants
Active Trials by Phase
Phase 3
5
Phase 2
5
Phase 1/2
3
Phase 1
7
Not specified
6
Active Trials — top 25 of 26
NCT IDTitleConditionStatus
Phase 3
NCT07181109 Zilebesiran in Patients With Hypertension Not Adequately Controlled and With Either… High Risk Cardiovascular Disease Recruiting
NCT07052903 TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With… Transthyretin Amyloidosis With Cardiomyopathy Recruiting
NCT07223203 TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With… Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy Recruiting
NCT04153149 HELIOS-B: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With… Transthyretin Amyloidosis (ATTR) With Cardiomyopathy Active, Not Recruiting
NCT06679946 A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With… Transthyretin Amyloidosis (ATTR) With Cardiomyopathy Enrolling by Invitation
Phase 2
NCT06393712 A Phase 2 Trial of ALN-APP in Patients With Cerebral Amyloid Angiopathy Cerebral Amyloid Angiopathy Recruiting
NCT07465224 A Study to Evaluate ALN-4324 on Insulin Sensitivity in Adults With Type 2 Diabetes… Type 2 Diabetes Mellitus (T2DM) Recruiting
NCT07575308 HMBeacon: A Phase 2 Study to Evaluate ALN-6400 in Adult and Adolescent Female Patients… Von Willebrand Disease (VWD) Recruiting
NCT07636811 A Study to Evaluate Mivelsiran in Adult Participants With Early-Stage Down… Down Syndrome-Associated Alzheimer's Disease (DS-AD) Recruiting
NCT07553442 A Study to Evaluate ALN-AGT01 RVR in Adult Patients With Mild to Moderate Hypertension… Hypertension Recruiting
Phase 1/2
NCT07463846 A Study to Evaluate ALN-2232 in Participants With Obesity Obesity Recruiting
NCT06659640 A Study to Evaluate ALN-6400 in Healthy Volunteers and Patients With Hereditary… Hereditary Hemorrhagic Telangiectasia Active, Not Recruiting
NCT06845202 A Study to Evaluate ALN-4324 in Overweight to Obese Healthy Volunteers and in Overweight… Obese or Overweight Healthy Volunteers Active, Not Recruiting
Phase 1
NCT06600321 A Study to Evaluate ALN-BCAT in Patients With Hepatocellular Carcinoma Advanced Hepatocellular Carcinoma Recruiting
NCT05231785 A Study to Evaluate the Safety and Tolerability of ALN-APP in Patients With EOAD Early-Onset Alzheimer Disease Recruiting
NCT06585449 A Study to Evaluate ALN-HTT02 in Adult Patients With Huntington's Disease Huntington's Disease Recruiting
NCT07295717 A Study to Evaluate ALN-4285 in Adult Healthy Volunteers Healthy Volunteers Recruiting
NCT07535606 A Study to Evaluate ALN-4915 in Adult Healthy Volunteers Healthy Volunteers Recruiting
NCT07624071 A Study to Evaluate ALN-6222 in Participants With Obesity Obesity Recruiting
NCT07214727 A Study to Evaluate ALN-5288 in Patients With Alzheimer's Disease Alzheimer's Disease Recruiting
Not specified
NCT07358078 DemonsTTRate: A Global, Observational, Multicenter, Long-term Study of Patients With… Transthyretin Amyloidosis With Cardiomyopathy Recruiting
NCT04883905 ELEVATE, a Registry of Patients With Acute Hepatic Porphyria (AHP) Acute Hepatic Porphyria Recruiting
NCT04561518 ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated… Transthyretin-Mediated Amyloidosis Recruiting
NCT05040373 Patisiran-Lipid Nanoparticle (LNP) Pregnancy Surveillance Program Hereditary Transthyretin-mediated (hATTR) Amyloidosis Recruiting
NCT04982393 BONAPH1DE, A Prospective Observational Study of Patients With Primary Hyperoxaluria Type… Primary Hyperoxaluria Type 1 Active, Not Recruiting
See all 26 active Alnylam Pharmaceuticals trials with filters →
Disease Areas
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