Top sponsors: Assistance Publique - Hôpitaux de Paris (14) · AstraZeneca (12) · National Cancer Institute (NCI) (12) · Massachusetts General Hospital (10) · Alnylam Pharmaceuticals (8)

Narrower conditions

Active trials

• X-Linked Intellectual Disability 104
• Amyloid Neuropathies, Familial 102
• Spinocerebellar Degenerations 79
• Neurofibromatoses 78
• Hereditary Sensory and Motor Neuropathy 72
• Huntington's Disease 66
• Myotonic Dystrophy 52
• Hereditary Central Nervous System Demyelinating Diseases 38
• Tourette Syndrome 38
• Tuberous Sclerosis 36
• Hepatolenticular Degeneration 35
• Neuronal Ceroid-Lipofuscinoses 22

Show all 21

• Optic Atrophies, Hereditary 21
• Spinal Muscular Atrophies of Childhood 19
• Bulbo-Spinal Atrophy, X-Linked 15
• Myotonia Congenita 11
• Hereditary Sensory and Autonomic Neuropathies 7
• Cockayne Syndrome 5
• Alexander Disease 4
• Canavan Disease 4
• Pantothenate Kinase-Associated Neurodegeneration 3

• All Trials
• Recent Changes
• New entrants

Data updated daily from ClinicalTrials.gov.