Also listed under Brain Diseases, Metabolic, Inborn, Heredodegenerative Disorders, Nervous System, Leukoencephalopathies
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: Ionis Pharmaceuticals, Inc. (3) · Shenzhen Geno-Immune Medical Institute (3) · Assistance Publique - Hôpitaux de Paris (2) · Children's Hospital of Philadelphia (2) · Forge Biologics, Inc (2)
Data updated daily from ClinicalTrials.gov.