Also listed under Genetic Diseases, X-Linked
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: Ionis Pharmaceuticals, Inc. (2) · Children's Hospital of Philadelphia (1) · Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta (1) · Joanne Kurtzberg, MD (1) · Mehmet Incebıyik (1)
Data updated daily from ClinicalTrials.gov.