Top sponsors: National Institute of Allergy and Infectious Diseases (NIAID) (14) · Children's Hospital Medical Center, Cincinnati (7) · Sarepta Therapeutics, Inc. (7) · Lokman Hekim University (6) · Novo Nordisk A/S (6)

Narrower conditions

Active trials

• Duchenne Muscular Dystrophy 133
• X-Linked Intellectual Disability 104
• Fabry Disease 57
• Hemophilia B 53
• Granulomatous Disease, Chronic 24
• Ornithine Carbamoyltransferase Deficiency Disease 19
• Bulbo-Spinal Atrophy, X-Linked 15
• Simpson-Golabi-Behmel syndrome 13
• Dyskeratosis Congenita 9
• Wiskott-Aldrich Syndrome 8
• X-Linked Combined Immunodeficiency Diseases 8
• Choroideremia 7

Show all 21

• Pelizaeus-Merzbacher Disease 7
• Dent Disease 6
• Barth Syndrome 5
• Bruton type agammaglobulinemia 4
• Glycogen Storage Disease Type IIb 4
• Immune Dysregulation, Polyendocrinopathy, Enteropathy, X-Linked Syndrome 4
• Oculocerebrorenal Syndrome 4
• Arts syndrome 3
• Muscular Dystrophy, Emery-Dreifuss 3

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Data updated daily from ClinicalTrials.gov.