Also listed under Genetic Diseases, X-Linked, Spinal Muscular Atrophy
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: Novartis Pharmaceuticals (2) · AstraZeneca (1) · Celgene (1) · Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) (1) · Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta (1)
Data updated daily from ClinicalTrials.gov.