Also listed under Heredodegenerative Disorders, Nervous System
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: Children's Hospital of Philadelphia (2) · Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta (1) · Ionis Pharmaceuticals, Inc. (1)
Data updated daily from ClinicalTrials.gov.