| Phase 3 | 1 |
| NCT ID | Title | Condition | Status | Updated |
|---|---|---|---|---|
| Phase 3 | ||||
| NCT04293185 | A Study Evaluating Gene Therapy With BB305 Lentiviral Vector in Sickle Cell Disease | Sickle Cell Disease | Active, Not Recruiting | 2024-12-10 |
| Not specified | ||||
| NCT06224413 | A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With… | Cerebral Adrenoleukodystrophy (CALD) | Recruiting | 2025-07-02 |
| NCT06271512 | A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel | Beta-Thalassemia | Recruiting | 2025-02-11 |
| NCT02698579 | Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated… | Cerebral Adrenoleukodystrophy (CALD) | Active, Not Recruiting | 2026-09-14 |
| NCT02633943 | Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated… | Transfusion-dependent Beta-Thalassemia | Active, Not Recruiting | 2025-04-09 |
| NCT04628585 | Long-term Follow-up of Subjects with Sickle Cell Disease Treated with Ex Vivo Gene Therapy | Sickle Cell Disease | Enrolling by Invitation | 2025-03-20 |
Sickle Cell Disease (2) · Thalassemia (2)