Also listed under Basal Ganglia Diseases, Brain Diseases, Metabolic, Inborn, Heredodegenerative Disorders, Nervous System, Metal Metabolism, Inborn Errors, Movement Disorders
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: Fondation Ophtalmologique Adolphe de Rothschild (5) · Assiut University (3) · Orphalan (2) · Prime Medicine, Inc. (2) · Yale University (2)
Data updated daily from ClinicalTrials.gov.