Sponsor Pipeline

National Human Genome Research Institute (NHGRI) Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-06-12
34
Active Trials
27
Recruiting
10
Disease Areas
6
Changes, 30 Days
What Changed in the Last 30 Days
DetectedTrialChange
2026-06-11 NCT00837122
Genetics of Type 2 Diabetes in West Africans
Trial completed
2026-06-11 NCT00837122
Genetics of Type 2 Diabetes in West Africans
Enrollment reduced: 10000 -> 7418 participants
2026-05-21 NCT04316546
MK-7075 (Miransertib) in Proteus Syndrome
overall status: "Recruiting" → "Active Not Recruiting"
2026-05-21 NCT04316546
MK-7075 (Miransertib) in Proteus Syndrome
Enrollment reduced: 45 -> 38 participants
2026-05-16 NCT04419870
Acute Infection in Mitochondrial Disease: Metabolism, Infection and Immunity
date change Primary completion pushed: 2026-05-01 -> 2027-05-01
2026-05-16 NCT04419870
Acute Infection in Mitochondrial Disease: Metabolism, Infection and Immunity
date change Completion pushed: 2026-05-01 -> 2027-05-01
Active Trials by Phase
Phase 2
2
Not specified
32
Active Trials — top 25 of 34
NCT IDTitleConditionStatus
Phase 2
NCT06664814 An Open-Label Phase 2 Study of N-Acetyl-D-Mannosamine (ManNAc) in Subjects With Primary… Focal Segmental Glomerulosclerosis Recruiting
NCT04316546 MK-7075 (Miransertib) in Proteus Syndrome Proteus Syndrome Active, Not Recruiting
Not specified
NCT04049604 IDENTIFY Study: Natural History of Maternal Neoplasia Maternal Neoplasia Recruiting
NCT00605878 Studies of Skin Microbes in Healthy People and in People With Skin Conditions Eczema Recruiting
NCT02089789 Clinical and Basic Investigations Into Known and Suspected Congenital Disorders of… Congenital Disorders of Glycosylation Recruiting
NCT00369421 Diagnosis and Treatment of Patients With Inborn Errors of Metabolism Arterial Calcification Due to Deficiency of CD73 Recruiting
NCT02890342 Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia Metabolic Disease Recruiting
NCT04419870 Acute Infection in Mitochondrial Disease: Metabolism, Infection and Immunity Mitochondrial Disease Recruiting
NCT06552754 Cybersickness Prevention and Mitigation in Virtual Reality for Healthy Volunteers Healthy Volunteers Recruiting
NCT06778239 Childhood-Onset Essential Hypertension Natural History Study Hypertension Recruiting
NCT06944067 Study to Understand the Genetic Risk of Developing an Immune Response After Blood… Sickle Cell Disease Recruiting
NCT00001456 Clinical and Basic Investigations Into Hermansky-Pudlak Syndrome Hermansky-Pudlak Syndrome (HPS) Recruiting
NCT00029965 Natural History of Glycosphingolipid Storage Disorders and Glycoprotein Disorders Neurological Regression Recruiting
NCT00359684 Use of Cysteamine in the Treatment of Cystinosis Cystinosis Recruiting
NCT00005917 Study of Chediak-Higashi Syndrome Chediak-Higashi Syndrome Recruiting
NCT00001373 Familial Mediterranean Fever and Related Disorders: Genetics and Disease Characteristics Familial Mediterranean Fever (FMF) Recruiting
NCT00005909 Study of Alkaptonuria Alkaptonuria Recruiting
NCT01780168 The NIH MINI Study: Metabolism, Infection, and Immunity in Inborn Errors of Metabolism Oxidative Phosphorylation Deficiencies Recruiting
NCT02595957 Genomic Services Research Program Colon Cancer Recruiting
NCT05007990 Caregiving Networks Across Disease Context and the Life Course Inherited Metabolic Disorders Recruiting
NCT03854318 Longitudinal Studies of Patient With FPDMM Inherited Hematological Diseases Recruiting
NCT00001403 Study of Proteus Syndrome and Related Congenital Disorders Proteus Syndrome Recruiting
NCT00078078 Clinical and Laboratory Study of Methylmalonic Acidemia Organic Acidemia Recruiting
NCT01087320 Genome Medical Sequencing for Gene Discovery Intellectual Disabilities Recruiting
NCT02450851 Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the… Genetic Disease Recruiting
View all 34 active National Human Genome Research Institute (NHGRI) trials with filters →
Disease Areas
Get alerts when National Human Genome Research Institute (NHGRI)'s trials change
Status changes, date slips, and new filings — detected daily, delivered to your inbox.
Start monitoring free