Sponsor Pipeline

Vertex Pharmaceuticals Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-06-12
33
Active Trials
17
Recruiting
17
Phase 3
7
Disease Areas
25
Changes, 30 Days
What Changed in the Last 30 Days
DetectedTrialChange
2026-06-09 NCT06185764
A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)
Enrollment increased: 44 -> 52 participants
2026-06-09 NCT06185764
A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)
date change Primary completion pushed: 2026-12-22 -> 2027-02-02
2026-06-09 NCT06185764
A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)
date change Completion pushed: 2026-12-22 -> 2027-02-02
2026-06-09 NCT07584434
A Phase 1, First-in-human Study of VX-433
Recruitment opened
2026-06-06 NCT07204275
Evaluation of Efficacy, Safety, and Tolerability of Povetacicept in Participants With…
Trial sites expanded: 93 -> 98 locations
2026-06-05 NCT05791201
A Safety, Tolerability, and Efficacy Study of VX-264 in Participants With Type 1 Diabetes
Primary endpoint(s) modified
2026-06-05 NCT05791201
A Safety, Tolerability, and Efficacy Study of VX-264 in Participants With Type 1 Diabetes
date change Primary completion pushed: 2026-05-29 -> 2027-03-12
2026-06-05 NCT05791201
A Safety, Tolerability, and Efficacy Study of VX-264 in Participants With Type 1 Diabetes
date change Completion pushed: 2026-05-29 -> 2027-03-12
2026-06-03 NCT07570069
Effects of Efavirenz on the Pharmacokinetics of Suzetrigine in Healthy Participants
Recruitment opened
2026-06-02 NCT06619860
Evaluation of Efficacy and Safety of VX-993 for Pain Associated With Diabetic Peripheral…
date change Primary completion pushed: 2026-04-30 -> 2027-03-25
2026-06-02 NCT06619860
Evaluation of Efficacy and Safety of VX-993 for Pain Associated With Diabetic Peripheral…
date change Completion pushed: 2026-05-30 -> 2027-04-22
2026-05-29 NCT05422222
Evaluation of VX-121/Tezacaftor/Deutivacaftor in Cystic Fibrosis (CF) Participants 1…
overall status: "Recruiting" → "Active Not Recruiting"
2026-05-27 NCT06154447
Evaluation of VX-828 in Healthy Participants and in Participants With Cystic Fibrosis
overall status: "Recruiting" → "Active Not Recruiting"
2026-05-27 NCT06154447
Evaluation of VX-828 in Healthy Participants and in Participants With Cystic Fibrosis
Enrollment reduced: 255 -> 165 participants
2026-05-27 NCT06154447
Evaluation of VX-828 in Healthy Participants and in Participants With Cystic Fibrosis
date change Primary completion pushed: 2026-04-23 -> 2026-07-16
2026-05-27 NCT06154447
Evaluation of VX-828 in Healthy Participants and in Participants With Cystic Fibrosis
date change Completion pushed: 2026-04-23 -> 2026-07-16
2026-05-23 NCT05668741
A Phase 1/2 Study of VX-522 in Participants With Cystic Fibrosis (CF)
overall status: "Recruiting" → "Active Not Recruiting"
2026-05-23 NCT05668741
A Phase 1/2 Study of VX-522 in Participants With Cystic Fibrosis (CF)
Enrollment reduced: 39 -> 26 participants
2026-05-23 NCT05668741
A Phase 1/2 Study of VX-522 in Participants With Cystic Fibrosis (CF)
Trial sites reduced: 43 -> 26 locations
2026-05-23 NCT05668741
A Phase 1/2 Study of VX-522 in Participants With Cystic Fibrosis (CF)
date change Primary completion moved earlier: 2026-12-23 -> 2026-04-21
Showing 20 of 25 changes detected in the last 30 days.
Active Trials by Phase
Phase 4
1
Phase 3
15
Phase 2/3
2
Phase 2
5
Phase 1/2
3
Phase 1
6
Not specified
1
Active Trials — top 25 of 33
NCT IDTitleConditionStatus
Phase 4
NCT07538570 Evaluation of Pain Treatment After Total Knee Arthroplasty Pain Recruiting
Phase 3
NCT04786262 A Safety, Tolerability, and Efficacy Study of VX-880 in Participants With Type 1 Diabetes Diabetes Mellitus, Type 1 Recruiting
NCT05477563 Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With… Beta-Thalassemia Recruiting
NCT06832410 An Efficacy, Safety, and Tolerability Study of VX-880 in Participants With Type 1… Type 1 Diabetes Recruiting
NCT06628908 Evaluation of Efficacy and Safety of Suzetrigine for Pain Associated With Diabetic… Diabetic Peripheral Neuropathic Pain Recruiting
NCT07231419 Evaluation of Efficacy and Safety of Suzetrigine (SUZ) for Pain Associated With Diabetic… Diabetic Peripheral Neuropathic Pain Recruiting
NCT05356195 Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With… Beta-Thalassemia Active, Not Recruiting
NCT05329649 Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Severe Sickle… Sickle Cell Disease Active, Not Recruiting
NCT04208529 A Long-term Follow-up Study in Participants Who Received CTX001 Beta-Thalassemia Enrolling by Invitation
NCT05844449 Evaluation of Long-Term Safety and Efficacy of Vanzacaftor/Tezacaftor/Deutivacaftor in… Cystic Fibrosis Enrolling by Invitation
NCT05444257 A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination Therapy Cystic Fibrosis Active, Not Recruiting
NCT06564142 Evaluation of Efficacy of Povetacicept in Adults With Immunoglobulin A Nephropathy (IgAN) Immunoglobulin A Nephropathy Active, Not Recruiting
NCT06696443 Evaluation of the Long-term Safety and Effectiveness of Suzetrigine (SUZ) in Participants… Diabetic Peripheral Neuropathic Pain Active, Not Recruiting
NCT05422222 Evaluation of VX-121/Tezacaftor/Deutivacaftor in Cystic Fibrosis (CF) Participants 1… Cystic Fibrosis Active, Not Recruiting
NCT05331183 Study to Evaluate Elexacaftor/Tezacaftor/Ivacaftor (ELX/TEZ/IVA) Long-term Safety and… Cystic Fibrosis Active, Not Recruiting
NCT06460506 Evaluation of Long-term Safety and Efficacy of ELX/TEZ/IVA in Cystic Fibrosis… Cystic Fibrosis Active, Not Recruiting
Phase 2/3
NCT05312879 Phase 2/3 Adaptive Study of VX-147 in Adult and Pediatric Participants With… Proteinuric Kidney Disease Recruiting
NCT07204275 Evaluation of Efficacy, Safety, and Tolerability of Povetacicept in Participants With… Primary Membranous Nephropathy Recruiting
Phase 2
NCT07161037 Phase 2a Study of VX-407 in Participants With ADPKD Who Have a Subset of PKD1 Gene… Autosomal Dominant Polycystic Kidney Disease (ADPKD) Recruiting
NCT07501702 A Phase 2 Study to Evaluate Povetacicept in Adults With Generalized Myasthenia Gravis Myasthenia Gravis, Generalized Recruiting
NCT06619860 Evaluation of Efficacy and Safety of VX-993 for Pain Associated With Diabetic Peripheral… Diabetic Peripheral Neuropathic Pain Recruiting
NCT06794996 Inaxaplin in Participants With Proteinuric APOL1 Mediated Kidney Disease With or Without… Proteinuric Kidney Disease Active, Not Recruiting
NCT06926621 A Study of Long-term Safety and Efficacy of VX-670 in Participants With Myotonic… Myotonic Dystrophy Type 1 (DM1) Enrolling by Invitation
Phase 1/2
NCT06185764 A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1) Myotonic Dystrophy Type 1 (DM1) Recruiting
NCT05668741 A Phase 1/2 Study of VX-522 in Participants With Cystic Fibrosis (CF) Cystic Fibrosis Active, Not Recruiting
View all 33 active Vertex Pharmaceuticals trials with filters →
Disease Areas
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