| NCT Number | NCT06185764 |
| Lead Sponsor | Vertex Pharmaceuticals Incorporated |
| Conditions | Myotonic Dystrophy Type 1 (DM1) |
| Enrollment | 52 participants |
| Start Date | 2024-02-20 |
| Primary Completion | 2027-02-02 (estimated) |
| Study Completion | 2027-02-02 (estimated) |
| Updated on ClinicalTrials.gov | 2026-06-08 |