Drug Pipeline

DFMO Clinical Trials

Data updated daily from ClinicalTrials.gov — last refresh 2026-06-12
12
Active Studies
10
Recruiting
8
Top Sponsors
3
Changes, 30 Days
What Changed in the Last 30 Days
DetectedTrialChange
2026-06-04 NCT06465199
Eflornithine (DFMO) and AMXT 1501 for Neuroblastoma, CNS Tumors, and Sarcomas
date change Primary completion pushed: 2033-02 -> 2033-05
2026-06-04 NCT06465199
Eflornithine (DFMO) and AMXT 1501 for Neuroblastoma, CNS Tumors, and Sarcomas
date change Completion pushed: 2035-02 -> 2035-05
2026-05-27 NCT07321912
Eflornithine (DFMO) for Ewing Sarcoma and Osteosarcoma
Recruitment opened
Active Studies by Phase
Phase 2
8
Phase 1/2
4
Active Trials
NCT IDTitleConditionStatus
Phase 2
NCT06059118 Difluoromethylornithine and High Dose Testosterone With Enzalutamide in Metastatic… Prostate Cancer Recruiting
NCT02679144 Neuroblastoma Maintenance Therapy Trial Neuroblastoma Recruiting
NCT04301843 Eflornithine (DFMO) and Etoposide for Relapsed/Refractory Neuroblastoma Neuroblastoma Recruiting
NCT05594563 TArgeting Type 1 Diabetes Using POLyamines (TADPOL) Type 1 Diabetes Recruiting
NCT02559778 Pediatric Precision Laboratory Advanced Neuroblastoma Therapy Neuroblastoma Recruiting
NCT04696029 DFMO as Maintenance Therapy for Molecular High/Very High Risk and Relapsed Medulloblastoma Medulloblastoma Recruiting
NCT07321912 Eflornithine (DFMO) for Ewing Sarcoma and Osteosarcoma Osteosarcoma Recruiting
NCT03794349 Irinotecan Hydrochloride, Temozolomide, and Dinutuximab With or Without Eflornithine in… High Risk Neuroblastoma Active, Not Recruiting
Phase 1/2
NCT07287917 Study of AMXT 1501 and DFMO in Combination With Standard Therapies in Advanced Solid… Melanoma (Skin Cancer) Recruiting
NCT06892678 DFMO Maintenance for Patients With Relapsed/Refractory Ewing Sarcoma or Osteosarcoma Osteosarcoma Recurrent Recruiting
NCT06465199 Eflornithine (DFMO) and AMXT 1501 for Neuroblastoma, CNS Tumors, and Sarcomas Atypical Teratoid/Rhabdoid Tumor Recruiting
NCT07468136 Retifanlimab With or Without Difluoromethylornithine for the Treatment of Progressive… Anaplastic Oligodendroglioma Not Yet Recruiting
Sponsors Running DFMO Trials
Disease Areas
Get alerts when DFMO trials change
Status changes, date slips, and new filings — detected daily, delivered to your inbox.
Start monitoring free