Sponsor Pipeline

Children's Hospital of Philadelphia Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-06-12
57
Active Trials
40
Recruiting
10
Disease Areas
2
Changes, 30 Days
What Changed in the Last 30 Days
DetectedTrialChange
2026-05-19 NCT07084129
Vancomycin and Acute Kidney Injury in Sepsis Treatment - Intervention
date change Primary completion pushed: 2026-08-15 -> 2027-05-15
2026-05-19 NCT07084129
Vancomycin and Acute Kidney Injury in Sepsis Treatment - Intervention
date change Completion pushed: 2026-12-31 -> 2027-05-31
New Trial Filings, Last 30 Days
First PostedTrialPhaseStatus
2026-06-09 NCT07635030 GABA and GSH in FRDA Enrolling by Invitation
Active Trials by Phase
Phase 2
6
Phase 1/2
5
Phase 1
3
Early Phase 1
6
Not specified
37
Active Trials — top 25 of 57
NCT IDTitleConditionStatus
Phase 2
NCT07123961 Pediatric Acute Respiratory Distress Syndrome (ARDS) Management Trial Acute Respiratory Distress Syndrome (ARDS) Recruiting
NCT06458036 Selpercatinib Pre-RAI in Patients With RET Fusion Thyroid Cancer (RAISE) Differentiated Thyroid Cancer Recruiting
NCT06693752 CEUS Evaluation of Hydrocephalus in Neonates and Infants Hydrocephalus in Infants Recruiting
NCT07543822 24VA022; VATCH Alpelisib for TIE2/PIK3CA Pathway VAs Vascular Anomalies Active, Not Recruiting
NCT07549646 24VA021; VATCH Trametinib for Ras/MAPK Pathway VAs Ras/MAPK Pathway Vascular Anomalies Active, Not Recruiting
NCT01050855 Reduced Intensity Conditioning (RIC) Regimen for Patients With Non-malignant Disorders Non Malignant Diseases Active, Not Recruiting
Phase 1/2
NCT06839976 CD19-Directed Chimeric Antigen Receptor Autologous T Cells (CART19) for Lupus SLE Recruiting
NCT05918640 Lurbinectedin in FET-Fused Tumors Ewing Sarcoma Recruiting
NCT06364774 ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia Beta-Thalassemia Recruiting
NCT06839456 Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post… Leukemia Recruiting
NCT04156893 RH Genotype Matched RBC Transfusions Sickle Cells Disease Recruiting
Phase 1
NCT06819683 Validation of Nanosensor Oxygen Measurement MItochondrial Myopathies Recruiting
NCT04086329 Validation of Oxygen Nanosensor in Mitochondrial Myopathy Mitochondrial Myopathies Recruiting
NCT07084129 Vancomycin and Acute Kidney Injury in Sepsis Treatment - Intervention Sepsis Recruiting
Early Phase 1
NCT02356653 Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC Leukemia Recruiting
NCT03107520 Intraoperative Contrast-Enhanced Ultrasound Evaluation of Blood Flow at the Time of… Developmental Dysplasia of the Hip Recruiting
NCT03810651 Pencil Beam Scanning in Patients With Renal Tumors Renal Tumor Recruiting
NCT05555550 Evaluation of 18F-Fluciclovine Positron Emission Tomography - Magnetic Resonance Imaging… Glioma Recruiting
NCT04293042 Treatment of BK Virus Infection With CTL Cells in Immunocompromised Transplant Patients BK Polyomavirus Recruiting
NCT02928991 Fludarabine Based RIC for Bone Marrow Failure Syndromes Bone Marrow Failure Syndromes Active, Not Recruiting
Not specified
NCT02493478 Improving Safety and Quality of Tracheal Intubation Practice in Pediatric ICUs Failed or Difficult Intubation, Sequela Recruiting
NCT06208852 Virtual Patient Navigation During a Pandemic Post-partum Depression Recruiting
NCT02714764 Evaluation of Outcome Metrics in Alexander Disease Alexander Disease Recruiting
NCT06890520 Neurometabolic Profile of Individuals With Primary Mitochondrial Disease Primary Mitochondrial Disease Recruiting
NCT05880199 BSGM to Evaluate Patients With GI Symptoms Gastrointestinal Motility Disorders in Children Recruiting
View all 57 active Children's Hospital of Philadelphia trials with filters →
Disease Areas
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