| Phase 1 | 1 | |
| Phase 1/2 | 2 | |
| Phase 2 | 1 |
| NCT ID | Title | Condition | Status | Updated |
|---|---|---|---|---|
| Phase 2 | ||||
| NCT07721025 | Study of LX2006 Gene Therapy in Friedreich Ataxia Cardiomyopathy | Friedreich Ataxia | Recruiting | 2026-09-02 |
| Phase 1/2 | ||||
| NCT05445323 | Gene Therapy for Cardiomyopathy Associated With Friedreich's Ataxia | Friedreich Ataxia | Active, Not Recruiting | 2025-12-23 |
| NCT06109181 | Gene Therapy for ACM Due to a PKP2 Pathogenic Variant | Arrhythmogenic Cardiomyopathy | Active, Not Recruiting | 2025-11-12 |
| Phase 1 | ||||
| NCT05400330 | Long-Term Follow-up of Gene Therapy for APOE4 Homozygote Alzheimer's Disease | Alzheimer Disease | Active, Not Recruiting | 2025-07-01 |
| Not specified | ||||
| NCT06865482 | Clinical Course Of Disease In Participants With FA-CM | Friedreich Ataxia | Recruiting | 2026-09-02 |
| NCT06976606 | A Study to Assess Real-world Patient Characteristics and Clinical Course for Symptomatic… | Arrhythmogenic Cardiomyopathy | Recruiting | 2025-05-16 |
| NCT07050160 | Long-term Follow-up Study of Gene Therapy for Arrhythmogenic Cardiomyopathy Due to a… | Arrhythmogenic Cardiomyopathy | Enrolling by Invitation | 2025-11-12 |
Heart Disease (6) · Alzheimer's Disease (1) · Dementia (1)