Clinical Trial

Study of LX2006 Gene Therapy in Friedreich Ataxia Cardiomyopathy

Study acronym: SUNRISE-FA 2
Recruiting Phase 2
View on ClinicalTrials.gov →
Summary
The purpose of Study LX2006-03, a multicenter, Phase 2, open-label, randomized, controlled study, is to evaluate the efficacy and safety of LX2006 gene therapy in participants with Friedreich ataxia (FA) cardiomyopathy (CM).
Trial Details
NCT Number NCT07721025
Lead Sponsor Lexeo Therapeutics
Conditions Friedreich Ataxia, Cardiomyopathy, Secondary
Enrollment 26 participants
Start Date 2026-06-25
Primary Completion 2032-06 (estimated)
Study Completion 2032-06 (estimated)
Updated on ClinicalTrials.gov 2026-07-22