Sponsor Pipeline

UniQure Biopharma B.V. Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-08-16
5
Active Trials
2
Recruiting
3
Disease Areas
Active Trials by Phase
Phase 1/2
5
Active Trials
NCT IDTitleConditionStatus
Phase 1/2
NCT06270316 Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease Fabry Disease Recruiting
NCT06063850 AMT-260 Gene Therapy Study in Adults With Unilateral Refractory Mesial Temporal Lobe… Mesial Temporal Lobe Epilepsy Recruiting
NCT05243017 Safety and Efficacy of AMT-130 in European Adults With Early Manifest Huntington's Disease Huntington Disease Active, Not Recruiting
NCT04120493 Safety and Proof-of-Concept (POC) Study With AMT-130 in Adults With Early Manifest… Huntington's Disease Active, Not Recruiting
NCT06100276 Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene… Amyotrophic Lateral Sclerosis Active, Not Recruiting
Disease Areas
Huntington's Disease (2) Epilepsy (1) ALS (1)
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