| Detected | Trial | Change |
|---|---|---|
| 2026-08-12 | NCT06131983 Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular… |
Primary endpoint(s) modified |
| 2026-08-12 | NCT06131983 Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular… |
Sponsor changed: Arrowhead Pharmaceuticals -> Sarepta Therapeutics, Inc. |
| 2026-08-12 | NCT06131983 Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular… |
date change Primary completion pushed: 2026-12 -> 2028-12-31 |
| 2026-08-12 | NCT06131983 Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular… |
date change Completion pushed: 2026-12 -> 2028-12-31 |
| 2026-08-12 | NCT06138743 Study of SRP-1003 in Participants With Type 1 Myotonic Dystrophy |
Primary endpoint(s) modified |
| 2026-08-12 | NCT06138743 Study of SRP-1003 in Participants With Type 1 Myotonic Dystrophy |
Sponsor changed: Arrowhead Pharmaceuticals -> Sarepta Therapeutics, Inc. |
| 2026-08-12 | NCT06138743 Study of SRP-1003 in Participants With Type 1 Myotonic Dystrophy |
Trial sites expanded: 11 -> 35 locations |
| 2026-08-12 | NCT06138743 Study of SRP-1003 in Participants With Type 1 Myotonic Dystrophy |
date change Primary completion pushed: 2026-12 -> 2026-12-31 |
| 2026-08-12 | NCT06138743 Study of SRP-1003 in Participants With Type 1 Myotonic Dystrophy |
date change Completion pushed: 2026-12 -> 2026-12-31 |
| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 4 | |||
| NCT07542314 | Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne… | Duchenne Muscular Dystrophy | Not Yet Recruiting |
| Phase 3 | |||
| NCT05967351 | A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec… | Duchenne Muscular Dystrophy | Enrolling by Invitation |
| NCT03992430 | A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With… | Muscular Dystrophy, Duchenne | Active, Not Recruiting |
| NCT06246513 | A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene… | Limb-girdle Muscular Dystrophy | Active, Not Recruiting |
| NCT05881408 | A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene… | Duchenne Muscular Dystrophy | Active, Not Recruiting |
| Phase 1/2 | |||
| NCT06131983 | Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular… | Muscular Dystrophy, Facioscapulohumeral | Recruiting |
| NCT06138743 | Study of SRP-1003 in Participants With Type 1 Myotonic Dystrophy | Myotonic Dystrophy 1 | Recruiting |
| Phase 1 | |||
| NCT07536061 | A First-in-human Study of the Effects of SRP-1005 in Participants With Huntington's… | Huntington's Disease | Recruiting |
| NCT04626674 | A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From… | Duchenne Muscular Dystrophy | Recruiting |
| NCT05876780 | A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of… | Limb Girdle Muscular Dystrophy | Active, Not Recruiting |
| Not specified | |||
| NCT06606340 | A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in… | Duchenne Muscular Dystrophy | Enrolling by Invitation |
| NCT04475926 | A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and… | Limb-girdle Muscular Dystrophy | Active, Not Recruiting |
| NCT06270719 | An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of… | Duchenne Muscular Dystrophy | Enrolling by Invitation |