Sponsor pipeline

Sarepta Therapeutics, Inc. clinical trial pipeline

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13 active trials 4 recruiting 4 Phase 3 2 disease areas 1 changes in 30 days

Data updated daily from ClinicalTrials.gov, last refresh 2026-10-02

What changed in the last 30 days

2026-09-12
Trial sites expanded: 7 → 12 locations
NCT04626674 A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From… · Phase 1

Active trials by phase

Phase 1
3
Phase 1/2
2
Phase 3
4
Phase 4
1
Not charted: 3 active trials with no phase listed on ClinicalTrials.gov (typically behavioural, device, procedure and observational studies).

Active trials

NCT IDTitleConditionStatusUpdated
Phase 4
NCT07542314 Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne… Duchenne Muscular Dystrophy Not Yet Recruiting 2026-08-27
Phase 3
NCT05881408 A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene… Duchenne Muscular Dystrophy Active, Not Recruiting 2026-05-22
NCT06246513 A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene… Limb-girdle Muscular Dystrophy Active, Not Recruiting 2026-03-02
NCT03992430 A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With… Muscular Dystrophy, Duchenne Active, Not Recruiting 2026-02-27
NCT05967351 A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec… Duchenne Muscular Dystrophy Enrolling by Invitation 2026-02-06
Phase 1/2
NCT06131983 Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular… Muscular Dystrophy, Facioscapulohumeral Recruiting 2026-08-11
NCT06138743 Study of SRP-1003 in Participants With Type 1 Myotonic Dystrophy Myotonic Dystrophy 1 Recruiting 2026-08-11
Phase 1
NCT04626674 A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From… Duchenne Muscular Dystrophy Recruiting 2026-09-11
NCT07536061 A First-in-human Study of the Effects of SRP-1005 in Participants With Huntington's… Huntington's Disease Recruiting 2026-09-04
NCT05876780 A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of… Limb Girdle Muscular Dystrophy Active, Not Recruiting 2026-02-19
Not specified
NCT06270719 An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of… Duchenne Muscular Dystrophy Enrolling by Invitation 2026-05-04
NCT04475926 A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and… Limb-girdle Muscular Dystrophy Active, Not Recruiting 2025-11-06
NCT06606340 A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in… Duchenne Muscular Dystrophy Enrolling by Invitation 2025-09-10

Disease areas by active trials

Duchenne Muscular Dystrophy (7) · Huntington's Disease (1)

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