Sponsor Pipeline

Hôpital Necker-Enfants Malades Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-08-16
6
Active Trials
2
Recruiting
1
Disease Areas
Active Trials by Phase
Not specified
6
Active Trials
NCT IDTitleConditionStatus
Not specified
NCT02965326 Surrogate Markers of Response to New Therapies in Cystic Fibrosis Patients Cystic Fibrosis Recruiting
NCT06682819 Metabolomics Analysis According to the Retinal Nerve Fiber Layer in Patients With NOHL… Healthy Subjects Recruiting
NCT06300567 Assessment of Patients Not Concluded After Neonatal Screening of Cystic Fibrosis. CFTR-RD Not Yet Recruiting
NCT07313085 Mechanisms of Fecal Incontinence in Wolfram Syndrome Wolfram Syndrome Not Yet Recruiting
NCT07336966 Does Recessive Optic Atrophy Due to WFS1 Exist? Wolfram Syndrome 1 Not Yet Recruiting
NCT07485413 Looking for VUS to Confirm Dominant Wolfram-like Syndrome Instead of Recessive Wolfram… Optical Coherence Tomography (OCT) of the Retina Active, Not Recruiting
Disease Areas
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