Drug Pipeline

Risdiplam Clinical Trials

Data updated daily from ClinicalTrials.gov — last refresh 2026-06-12
7
Active Studies
4
Recruiting
1
Phase 3
3
Top Sponsors
2
Changes, 30 Days
What Changed in the Last 30 Days
DetectedTrialChange
2026-06-12 NCT05115110
A Study to Investigate the Safety and Efficacy of RO7204239 in Combination With Risdiplam…
date change Primary completion moved earlier: 2029-02-27 -> 2026-10-28
2026-06-12 NCT05115110
A Study to Investigate the Safety and Efficacy of RO7204239 in Combination With Risdiplam…
date change Completion moved earlier: 2029-02-27 -> 2026-10-28
Active Studies by Phase
Phase 4
3
Phase 2/3
1
Phase 2
3
Active Trials
NCT IDTitleConditionStatus
Phase 4
NCT05861986 A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early… Muscular Atrophy, Spinal Recruiting
NCT05861999 A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric… Muscular Atrophy, Spinal Recruiting
NCT05232929 Long-term Follow-up Study of Risdiplam in Participants With Spinal Muscular Atrophy (SMA) Spinal Muscular Atrophy Active, Not Recruiting
Phase 2/3
NCT05115110 A Study to Investigate the Safety and Efficacy of RO7204239 in Combination With Risdiplam… Spinal Muscular Atrophy (SMA) Active, Not Recruiting
Phase 2
NCT07047144 A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and… Spinal Muscular Atrophy Recruiting
NCT05808764 A Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With… Muscular Atrophy, Spinal Recruiting
NCT03779334 A Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal… Muscular Atrophy, Spinal Active, Not Recruiting
Sponsors Running Risdiplam Trials
Disease Areas
Get alerts when Risdiplam trials change
Status changes, date slips, and new filings — detected daily, delivered to your inbox.
Start monitoring free