Track this trial free. DataLookout checks ClinicalTrials.gov daily and emails you which fields changed on NCT03779334 (status, enrollment, completion dates, endpoints, sites) when this record is updated. Free accounts track up to 5 trials.

Track this trial

A Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy

Study acronym: Rainbowfish
StatusActive, Not Recruiting
PhasePhase 2
Started2019-08-07
View on ClinicalTrials.gov ↗
A global study of oral risdiplam in pre-symptomatic participants with spinal muscular atrophy (SMA).

Amendment record

Amended 59 times since 2018-12-17; most recent filed 2026-07-08. The 50 most recent of 60 record versions are listed below. See every version on ClinicalTrials.gov ↗

Dates here are the day the sponsor filed the amendment, not the day ClinicalTrials.gov published it. Version history last read from ClinicalTrials.gov on 2026-08-31.

2026-07-08
Amendment Study Status v59
2026-04-07
Amendment Study Status v58
2026-01-07
Amendment Study Status v57
2025-11-20
Amendment Study Status v56
2025-08-22
Amendment Study Status v55
2025-05-26
Amendment Study Identification, Study Status, Outcome Measures (Results) v54
2025-03-05
Amendment Study Status, Contacts/Locations, IPDSharing v53
2024-12-05
Amendment Study Status v52
2024-09-05
Amendment Study Status v51
2024-06-07
Amendment Study Identification, Study Status v50
2024-03-12
Amendment Study Status, Study Description v49
2024-02-09
Amendment Study Status, Study Design, Arms and Interventions, Outcome Measures, Document Section, Participant Flow, Baseline Characteristics, Outcome Measures (Results), Adverse Events, More Information v48
2024-01-16
Amendment Study Status v47
2023-11-07
Amendment Study Status v46
2023-11-02
Amendment Study Status v45
2023-08-16
Amendment Study Status, Contacts/Locations v44
2023-05-22
Amendment Study Status v43
2023-03-09
Amendment Study Status, Contacts/Locations v42
2022-12-21
Amendment Study Status, Contacts/Locations v41
2022-09-29
Amendment Study Status, Contacts/Locations v40
2022-07-28
Amendment Study Status, Study Design, Contacts/Locations v39
2022-04-01
Amendment Study Status v38
2022-03-15
Amendment RecruitingActive, Not Recruiting Study Status, Contacts/Locations v37
2022-01-26
Amendment Study Status, Contacts/Locations v36
2021-12-20
Amendment Study Status, Contacts/Locations v35
2021-11-16
Amendment Study Status, Contacts/Locations v34
2021-10-10
Amendment Study Status, Contacts/Locations v33
2021-09-09
Amendment Study Status v32
2021-08-10
Amendment Study Status, Contacts/Locations v31
2021-07-06
Amendment Study Status, Contacts/Locations v30
2021-06-04
Amendment Study Status, Contacts/Locations v29
2021-05-04
Amendment Study Status, Study Description, Arms and Interventions, Outcome Measures, Contacts/Locations v28
2021-04-12
Amendment Study Status, Contacts/Locations v27
2021-03-12
Amendment Study Status, Contacts/Locations v26
2021-02-08
Amendment Study Status v25
2020-12-03
Amendment Study Status v24
2020-11-04
Amendment Study Status, Contacts/Locations v23
2020-10-05
Amendment Study Identification, Study Status, Study Description, Outcome Measures, Eligibility, Contacts/Locations, IPDSharing v22
2020-09-17
Amendment Study Status, Contacts/Locations v21
2020-08-04
Amendment Study Status, Contacts/Locations v20
2020-06-24
Amendment Study Status, Contacts/Locations v19
2020-06-01
Amendment Study Status, Contacts/Locations v18
2020-04-30
Amendment Study Status, Contacts/Locations v17
2020-03-23
Amendment Study Status, Contacts/Locations v16
2020-02-17
Amendment Study Status, Contacts/Locations v15
2020-02-05
Amendment Study Status v14
2020-01-09
Amendment Study Status, Contacts/Locations v13
2019-12-04
Amendment Study Status, Contacts/Locations v12
2019-10-24
Amendment Study Status v11
2019-09-23
Amendment Study Status, Contacts/Locations v10
Trial Details
NCT Number NCT03779334
Lead Sponsor Hoffmann-La Roche
Conditions Muscular Atrophy, Spinal
Enrollment 26 participants
Start Date 2019-08-07
Primary Completion 2023-02-20 (estimated)
Study Completion 2027-02-28 (estimated)
Updated on ClinicalTrials.gov 2026-07-09