Drug Pipeline

Mitapivat Clinical Trials

Data updated daily from ClinicalTrials.gov — last refresh 2026-06-12
10
Active Studies
0
Recruiting
7
Phase 3
2
Top Sponsors
Active Studies by Phase
Phase 4
1
Phase 3
6
Phase 2/3
1
Phase 2
1
Phase 1/2
1
Active Trials
NCT IDTitleConditionStatus
Phase 4
NCT05777993 A Study to Provide Continued Access to Mitapivat for Participants Who Previously… Pyruvate Kinase Deficiency Enrolling by Invitation
Phase 3
NCT07506863 A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in… Transfusion-dependent Alpha-Thalassemia Not Yet Recruiting
NCT07517133 A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in… Non-Transfusion-dependent Alpha-Thalassemia Not Yet Recruiting
NCT04770753 A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With… Non-Transfusion-dependent Alpha-Thalassemia Active, Not Recruiting
NCT04770779 A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With… Transfusion-dependent Alpha-Thalassemia Active, Not Recruiting
NCT05144256 A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With… Pediatric Pyruvate Kinase Deficiency Active, Not Recruiting
NCT05175105 A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With… Pediatric Pyruvate Kinase Deficiency Active, Not Recruiting
Phase 2/3
NCT05031780 A Study Evaluating the Efficacy and Safety of Mitapivat (AG-348) in Participants With… Sickle Cell Disease Active, Not Recruiting
Phase 2
NCT03692052 A Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of… Thalassemia Active, Not Recruiting
Phase 1/2
NCT04610866 Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Long-term Mitapivat… Sickle Cell Disease Active, Not Recruiting
Sponsors Running Mitapivat Trials
Disease Areas
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