Sponsor Pipeline

Agios Pharmaceuticals, Inc. Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-08-16
15
Active Trials
4
Recruiting
8
Phase 3
3
Disease Areas
7
Changes, 30 Days
What Changed in the Last 30 Days
DetectedTrialChange
2026-08-13 NCT05777993
A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an…
Primary endpoint(s) modified
2026-08-13 NCT05777993
A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an…
Enrollment increased: 6 -> 59 participants
2026-08-13 NCT05777993
A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an…
Trial sites expanded: 4 -> 23 locations
2026-08-05 NCT07656415
A Study to Investigate the Effect of Mitapivat on Transfusion Burden in Subjects With…
Recruitment opened
2026-08-05 NCT07656415
A Study to Investigate the Effect of Mitapivat on Transfusion Burden in Subjects With…
Trial sites expanded: 0 -> 3 locations
2026-08-04 NCT07517133
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in…
Recruitment opened
2026-08-04 NCT07506863
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in…
Recruitment opened
Active Trials by Phase
Phase 4
1
Phase 3
7
Phase 2/3
1
Phase 2
3
Phase 1
2
Not specified
1
Active Trials
NCT IDTitleConditionStatus
Phase 4
NCT05777993 A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an… Pyruvate Kinase Deficiency Enrolling by Invitation
Phase 3
NCT07506863 A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in… Transfusion-dependent Alpha-Thalassemia Recruiting
NCT07517133 A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in… Non-Transfusion-dependent Alpha-Thalassemia Recruiting
NCT07656415 A Study to Investigate the Effect of Mitapivat on Transfusion Burden in Subjects With… Sickle Cell Disease Recruiting
NCT05144256 A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With… Pediatric Pyruvate Kinase Deficiency Active, Not Recruiting
NCT05175105 A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With… Pediatric Pyruvate Kinase Deficiency Active, Not Recruiting
NCT04770753 A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With… Non-Transfusion-dependent Alpha-Thalassemia Active, Not Recruiting
NCT04770779 A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With… Transfusion-dependent Alpha-Thalassemia Active, Not Recruiting
Phase 2/3
NCT05031780 A Study Evaluating the Efficacy and Safety of Mitapivat (AG-348) in Participants With… Sickle Cell Disease Active, Not Recruiting
Phase 2
NCT03692052 A Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of… Thalassemia Active, Not Recruiting
NCT06924970 A Dose-Finding Study of Tebapivat to Assess Efficacy, and Safety in Participants With… Sickle Cell Disease Active, Not Recruiting
NCT05490446 A Study of Tebapivat (AG-946) in Participants With Anemia Due to Lower-Risk… Myelodysplastic Syndromes Active, Not Recruiting
Phase 1
NCT07241234 A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of… Phenylketonuria Recruiting
NCT07075640 A Study to Determine the Safety and Tolerability of AG-236 and How it is Absorbed, Broken… Healthy Participants Active, Not Recruiting
Not specified
NCT03481738 Pyruvate Kinase Deficiency Global Longitudinal Registry Pyruvate Kinase Deficiency Active, Not Recruiting
Disease Areas
Get alerts when Agios Pharmaceuticals, Inc.'s trials change
Status changes, date slips, and new filings — detected daily, delivered to your inbox.
Start monitoring free