Also listed under Mucopolysaccharidoses
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: JCR Pharmaceuticals Co., Ltd. (4) · Denali Therapeutics Inc. (3) · REGENXBIO Inc. (3) · Albert Einstein College of Medicine (1) · AO GENERIUM (1)
Data updated daily from ClinicalTrials.gov.