| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 3 | |||
| NCT05594992 | An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in MPS II… | Mucopolysaccharidosis II | Enrolling by Invitation |
| NCT04573023 | A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT) | Mucopolysaccharidosis II | Active, Not Recruiting |
| Phase 2/3 | |||
| NCT04348136 | An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type II | Mucopolysaccharidosis II | Active, Not Recruiting |
| Phase 2 | |||
| NCT03708965 | An Extension Study of JR-141-BR21 in Patients With Mucopolysaccharidosis II | Mucopolysaccharidosis II | Active, Not Recruiting |
| Phase 1/2 | |||
| NCT06488924 | An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB | Mucopolysaccharidosis III-B | Recruiting |
| NCT06095388 | Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA | Mucopolysaccharidosis III-A | Active, Not Recruiting |
| NCT07640984 | A Phase I/II Trial of JR-446 in Mucopolysaccharidosis Type IIIB (MPS IIIB) | Mucopolysaccharidosis IIIB | Not Yet Recruiting |
| Not specified | |||
| NCT07615400 | A Long-Term Observational Study of Patients With Fucosidosis | Fucosidosis | Recruiting |