Top sponsors: National Cancer Institute (NCI) (5) · Paul Szabolcs (3) · Rocket Pharmaceuticals Inc. (3) · Boston Children's Hospital (2) · Children's Hospital Medical Center, Cincinnati (2)

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Active trials

• Anemia, Hypoplastic, Congenital 29
• Dyskeratosis Congenita 9
• Neutropenia, Severe Congenital, Autosomal Recessive 3 6
• VLCAD deficiency 6
• Shwachman-Diamond Syndrome 5

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Data updated daily from ClinicalTrials.gov.