Also listed under Lipid Metabolism, Inborn Errors, Mitochondrial Diseases, Muscular Diseases
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: Ultragenyx Pharmaceutical Inc (2) · Children's National Research Institute (1) · LMU Klinikum (1) · Minovia Therapeutics Ltd. (1) · RTI International (1)
Data updated daily from ClinicalTrials.gov.