Disease Landscape

Huntington's Disease Clinical Trials

Data updated daily from ClinicalTrials.gov — last refresh 2026-08-16
64
Active Trials
38
Recruiting
7
Phase 3
52
Sponsors
17
Changes, 30 Days
What Changed in the Last 30 Days
DetectedTrialChange
2026-08-12 NCT07326709
A Study to Investigate the Efficacy, Safety and Tolerability of Votoplam in Participants… · Novartis Pharmaceuticals
Trial sites expanded: 51 -> 60 locations
2026-08-11 NCT06444217
Gene Therapy Development and Validation for Huntington's Disease Fibro TG-HD · University Hospital, Angers
Trial completed
2026-08-11 NCT06444217
Gene Therapy Development and Validation for Huntington's Disease Fibro TG-HD · University Hospital, Angers
date change Primary completion moved earlier: 2026-07-23 -> 2025-11-17
2026-08-11 NCT06444217
Gene Therapy Development and Validation for Huntington's Disease Fibro TG-HD · University Hospital, Angers
date change Completion moved earlier: 2028-07-23 -> 2025-11-17
2026-08-11 NCT06209515
Sociodemographic Factors and Criminal Behaviour Preceding Neurodegenerative Disease… · Kuopio University Hospital
date change Primary completion pushed: 2027-12-31 -> 2029-12-31
2026-08-11 NCT06209515
Sociodemographic Factors and Criminal Behaviour Preceding Neurodegenerative Disease… · Kuopio University Hospital
date change Completion pushed: 2027-12-31 -> 2029-12-31
2026-08-11 NCT05686551
GENERATION HD2. A Study to Evaluate the Safety, Biomarkers, and Efficacy of Tominersen… · Hoffmann-La Roche
date change Completion moved earlier: 2027-04-01 -> 2026-10-31
2026-08-08 NCT07609108
Pridopidine Phase 3 Study in Huntington's Disease · Prilenia
Recruitment opened
2026-08-08 NCT07609108
Pridopidine Phase 3 Study in Huntington's Disease · Prilenia
Trial sites expanded: 0 -> 66 locations
2026-08-06 NCT04713982
Impact of Deutetrabenazine on Functional Speech and Gait Dynamics in Huntington Disease · Vanderbilt University Medical Center
date change Primary completion pushed: 2026-06-30 -> 2027-06-30
2026-08-06 NCT04713982
Impact of Deutetrabenazine on Functional Speech and Gait Dynamics in Huntington Disease · Vanderbilt University Medical Center
date change Completion pushed: 2026-10-01 -> 2027-10-01
2026-08-04 NCT07246941
A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of… · Hoffmann-La Roche
Enrollment closed, study ongoing
2026-07-30 NCT07326709
A Study to Investigate the Efficacy, Safety and Tolerability of Votoplam in Participants… · Novartis Pharmaceuticals
Trial sites expanded: 41 -> 51 locations
2026-07-29 NCT06667414
Frequency of Selected Single Nucleotide Polymorphisms in Huntington Disease Gene… · Hoffmann-La Roche
Trial completed
2026-07-29 NCT06667414
Frequency of Selected Single Nucleotide Polymorphisms in Huntington Disease Gene… · Hoffmann-La Roche
date change Primary completion moved earlier: 2027-02-28 -> 2026-07-03
2026-07-29 NCT06667414
Frequency of Selected Single Nucleotide Polymorphisms in Huntington Disease Gene… · Hoffmann-La Roche
date change Completion moved earlier: 2027-02-28 -> 2026-07-03
2026-07-24 NCT07537075
An Extension of SKY-0515 in Participants With Huntington's Disease · Skyhawk Therapeutics, Inc.
Trial sites expanded: 4 -> 10 locations
New Sponsor Entrants, Last 90 Days
First PostedTrialSponsorPhase
2026-05-27 NCT07609108 Pridopidine Phase 3 Study in Huntington's Disease Prilenia NEW Phase 3
2026-05-22 NCT07601516 Real World Effectiveness and Safety of Deutetrabenazine in Adult Chinese Patients With… Teva Branded Pharmaceutical Products R&D LLC NEW Phase 4
Active Trials by Phase
Phase 3
3
Phase 2/3
4
Phase 2
5
Phase 1/2
7
Phase 1
4
Early Phase 1
1
Not specified
40
Active Trials — top 25 of 64
NCT IDTitleSponsorStatus
Phase 3
NCT07609108 Pridopidine Phase 3 Study in Huntington's Disease Prilenia Recruiting
NCT07326709 A Study to Investigate the Efficacy, Safety and Tolerability of Votoplam in Participants… Novartis Pharmaceuticals Recruiting
NCT06312189 Long-term Study to Evaluate Safety and Tolerability of Valbenazine in Participants With… Neurocrine Biosciences Enrolling by Invitation
Phase 2/3
NCT07378644 Study to Evaluate the Pharmacodynamics, Safety and Efficacy of SKY-0515 in Participants… Skyhawk Therapeutics, Inc. Recruiting
NCT06873334 Study of SKY-0515 for Safety, Efficacy, and Pharmacodynamics in Participants With… Skyhawk Therapeutics, Inc. Active, Not Recruiting
NCT07537075 An Extension of SKY-0515 in Participants With Huntington's Disease Skyhawk Therapeutics, Inc. Enrolling by Invitation
NCT04713982 Impact of Deutetrabenazine on Functional Speech and Gait Dynamics in Huntington Disease Vanderbilt University Medical Center Active, Not Recruiting
Phase 2
NCT04478734 Trial of the Combined Use of Thiamine and Biotin in Patients With Huntington's Disease Fundación Pública Andaluza para la gestión de la Investigación en Sevilla Recruiting
NCT05509153 A Randomised Controlled Trial, Of N-Acetyl Cysteine (NAC), for Premanifest Huntingtin… Western Sydney Local Health District Recruiting
NCT06853743 The NAD-HD Study: A Study to Investigate Efficacy and Safety of Nicotinamide Riboside… Oslo University Hospital Recruiting
NCT06254482 An Extension Study to Evaluate the Long-Term Safety and Efficacy of Votoplam in… Novartis Pharmaceuticals Active, Not Recruiting
NCT05686551 GENERATION HD2. A Study to Evaluate the Safety, Biomarkers, and Efficacy of Tominersen… Hoffmann-La Roche Active, Not Recruiting
Phase 1/2
NCT05822908 A Safety and Pharmacokinetics Trial of VO659 in SCA1, SCA3 and HD Vico Therapeutics B. V. Recruiting
NCT07451613 Safety and Tolerability Study of Human Neural Stem Cells for Huntington's Disease Leslie Thompson Recruiting
NCT06826612 A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease Hoffmann-La Roche Recruiting
NCT05243017 Safety and Efficacy of AMT-130 in European Adults With Early Manifest Huntington's Disease UniQure Biopharma B.V. Active, Not Recruiting
NCT04120493 Safety and Proof-of-Concept (POC) Study With AMT-130 in Adults With Early Manifest… UniQure Biopharma B.V. Active, Not Recruiting
NCT07339514 A Phase I Clinical Study of ER2001 Injection for the Treatment of Early Manifest… ExoRNA Bioscience Active, Not Recruiting
NCT05541627 A Study to Evaluate AB-1001 Striatal Administration in Adults With Early Manifest… AskBio France, SAS, a subsidiary of AskBio Inc. Active, Not Recruiting
Phase 1
NCT07536061 A First-in-human Study of the Effects of SRP-1005 in Participants With Huntington's… Sarepta Therapeutics, Inc. Recruiting
NCT06585449 A Study to Evaluate ALN-HTT02 in Adult Patients With Huntington's Disease Alnylam Pharmaceuticals Recruiting
NCT07516899 Mass Balance Study of [14C] LPM3770164 in Healthy Participants Luye Pharma Group Ltd. Not Yet Recruiting
NCT07246941 A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of… Hoffmann-La Roche Active, Not Recruiting
Early Phase 1
NCT06634628 iMagemHTT-009- FIH Evaluation of Novel Mutant Huntingtin PET Radioligand… CHDI Foundation, Inc. Recruiting
Not specified
NCT01574053 Enroll -HD: A Prospective Registry Study in a Global Huntington's Disease Cohort CHDI Foundation, Inc. Recruiting
See all 64 active Huntington's Disease trials with filters →
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