Clinical Trial

A Clinical Trial of Elsunersen in Pediatric SCN2A-DEE to Assess Efficacy and Safety

Recruiting Phase 3
View on ClinicalTrials.gov →
Summary
A Multi-Center, Single-Arm Clinical Trial to Investigate the Efficacy and Safety of Elsunersen in Pediatric Participants with Early Onset SCN2A Developmental and Epileptic Encephalopathy
Protocol Amendment History 4 changes
notable Primary completion pushed: 2026-06 -> 2026-12 2026-08-04
notable Enrollment reduced: 50 -> 40 participants 2026-05-28
minor Trial arms changed: 4 -> 3 2026-05-28
notable Trial sites expanded: 4 -> 10 locations 2026-05-28
Trial Details
NCT Number NCT07019922
Lead Sponsor Praxis Precision Medicines
Conditions Epileptic Encephalopathy, SCN2A Encephalopathy
Enrollment 40 participants
Start Date 2025-08-13
Primary Completion 2026-12 (estimated)
Study Completion 2028-12 (estimated)
Updated on ClinicalTrials.gov 2026-08-03