Sponsor Pipeline

Praxis Precision Medicines Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-08-16
8
Active Trials
2
Recruiting
6
Phase 3
1
Disease Areas
13
Changes, 30 Days
What Changed in the Last 30 Days
DetectedTrialChange
2026-08-11 NCT06999902
Double-blind, Randomized Trial of PRAX-628 in Adults With Focal Seizures to Evaluate…
Trial completed
2026-08-11 NCT06999902
Double-blind, Randomized Trial of PRAX-628 in Adults With Focal Seizures to Evaluate…
Enrollment increased: 230 -> 255 participants
2026-08-11 NCT06999902
Double-blind, Randomized Trial of PRAX-628 in Adults With Focal Seizures to Evaluate…
Trial sites expanded: 26 -> 69 locations
2026-08-11 NCT06999902
Double-blind, Randomized Trial of PRAX-628 in Adults With Focal Seizures to Evaluate…
date change Primary completion pushed: 2025-11-24 -> 2026-05-14
2026-08-11 NCT06999902
Double-blind, Randomized Trial of PRAX-628 in Adults With Focal Seizures to Evaluate…
date change Completion pushed: 2025-12-08 -> 2026-05-14
2026-08-05 NCT07010471
A Clinical Trial for Participants With DEE to Assess Efficacy, Safety, Tolerability, and…
Enrollment closed, study ongoing
2026-08-04 NCT07287163
Clinical Trial of Vormatrigine in Adult Patients With Epilepsy
Trial sites expanded: 20 -> 36 locations
2026-08-04 NCT07505004
Randomized Clinical Trial Evaluating the Efficacy and Safety of Vormatrigine in Adults…
Enrollment closed, study ongoing
2026-08-04 NCT05737784
A Clinical Trial of PRAX-222 in Pediatric Participants With Early Onset SCN2A…
Enrollment closed, study ongoing
2026-08-04 NCT05737784
A Clinical Trial of PRAX-222 in Pediatric Participants With Early Onset SCN2A…
date change Primary completion pushed: 2025-08 -> 2026-04-01
2026-08-04 NCT05737784
A Clinical Trial of PRAX-222 in Pediatric Participants With Early Onset SCN2A…
date change Completion pushed: 2027-09 -> 2028-02
2026-08-04 NCT07019922
A Clinical Trial of Elsunersen in Pediatric SCN2A-DEE to Assess Efficacy and Safety
date change Primary completion pushed: 2026-06 -> 2026-12
2026-08-04 NCT06840925
A Clinical Trial to Evaluate the Relative Bioavailability of PRAX-628
Completed without a posted recruiting period
Active Trials by Phase
Phase 3
5
Phase 2/3
1
Phase 2
1
Phase 1/2
1
Active Trials
NCT IDTitleConditionStatus
Phase 3
NCT07019922 A Clinical Trial of Elsunersen in Pediatric SCN2A-DEE to Assess Efficacy and Safety Epileptic Encephalopathy Recruiting
NCT06087276 Essential 3 - Decentralized, Phase 3 Study Evaluating the Safety and Efficacy of… Essential Tremor Active, Not Recruiting
NCT07287163 Clinical Trial of Vormatrigine in Adult Patients With Epilepsy Epilepsy, Tonic-Clonic Enrolling by Invitation
NCT07505004 Randomized Clinical Trial Evaluating the Efficacy and Safety of Vormatrigine in Adults… Focal Epilepsy Active, Not Recruiting
NCT07010471 A Clinical Trial for Participants With DEE to Assess Efficacy, Safety, Tolerability, and… Developmental and Epileptic Encephalopathy 1 Active, Not Recruiting
Phase 2/3
NCT05818553 A Clinical Trial of PRAX-562 in Subjects With Developmental and Epileptic… SCN2A Encephalopathy Active, Not Recruiting
Phase 2
NCT06908356 An Open Label Trial to Evaluate the Efficacy and Safety of PRAX-628 in Adults With Focal… Focal Onset Seizure Recruiting
Phase 1/2
NCT05737784 A Clinical Trial of PRAX-222 in Pediatric Participants With Early Onset SCN2A… SCN2A-DEE Active, Not Recruiting
Disease Areas
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