Clinical Trial

AMX0035 in Adult Patients With Wolfram Syndrome

Active, Not Recruiting Phase 2
View on ClinicalTrials.gov →
Summary
This study is an open label Phase II study to evaluate the safety and efficacy of AMX0035 in adults with Wolfram syndrome.
Protocol Amendment History 7 amendments
This ClinicalTrials.gov record has been amended 7 times since 2022-12-22; most recent amendment 2026-04-09.
Status change: Recruiting → Active, Not Recruiting 2024-04-25
Status change: Not Yet Recruiting → Recruiting 2023-03-14
Trial Details
NCT Number NCT05676034
Lead Sponsor Amylyx Pharmaceuticals Inc.
Conditions Wolfram Syndrome
Enrollment 12 participants
Start Date 2023-03-03
Primary Completion 2024-07-23 (estimated)
Study Completion 2028-05-31 (estimated)
Updated on ClinicalTrials.gov 2026-04-14