Clinical Trial

A Study of mRNA-3745 in Adult and Pediatric Participants With Glycogen Storage Disease Type 1a (GSD1a)

Active, Not Recruiting Phase 1/2
View on ClinicalTrials.gov →
Summary
The main goal of this trial is to evaluate the safety and tolerability of mRNA-3745 via intravenous (IV) administration in adult and pediatric participants with GSD1a.
Protocol Amendment History 19 amendments
This ClinicalTrials.gov record has been amended 19 times since 2021-10-14; most recent amendment 2025-12-09.
Status change: Recruiting → Active, Not Recruiting 2025-12-09
Status change: Not Yet Recruiting → Recruiting 2022-01-24
Trial Details
NCT Number NCT05095727
Lead Sponsor ModernaTX, Inc.
Conditions Glycogen Storage Disease
Enrollment 15 participants
Start Date 2022-06-01
Primary Completion 2026-11-30 (estimated)
Study Completion 2026-11-30 (estimated)
Updated on ClinicalTrials.gov 2025-12-15