Sponsor pipeline

X4 Pharmaceuticals clinical trial pipeline

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Data updated daily from ClinicalTrials.gov, last refresh 2026-10-16

Active trials by phase

Phase 3
1

Active trials

NCT IDTitleConditionStatusUpdated
Phase 3
NCT06056297 A Study of Mavorixafor in Participants With Congenital and Acquired Primary Autoimmune… Neutropenia Recruiting 2026-08-06

Disease areas by active trials

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