| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 3 | |||
| NCT07265232 | Real World Clinical Effectiveness & Safety of Vesemnogene Lantuparvovec for Spinal… | Spinal Muscular Atrophy (SMA) | Recruiting |
| Phase 1/2 | |||
| NCT06288230 | An Open Label Study of Gene Therapy Product (Vesemnogene Lantuparvovec) in Spinal… | Spinal Muscular Atrophy | Active, Not Recruiting |
| NCT06308159 | An Open-label Study of a Gene Therapy Product (Vebeglogene Autotemcel) in Transfusion… | Beta-Thalassemia | Active, Not Recruiting |