Clinical Trial

Advancing Integrated Therapies for Gaucher Disease

Recruiting
View on ClinicalTrials.gov →
Summary
The purpose of this study is to better understand the natural history, clinical outcomes, and biological features of Gaucher disease in patients receiving standard medical care
Trial Details
NCT Number NCT07758816
Lead Sponsor Yale University
Collaborators: Sanofi-Yale External Research Collaboration
Conditions Gaucher Disease
Enrollment 30 participants
Start Date 2026-05-06
Primary Completion 2030-09 (estimated)
Study Completion 2030-09 (estimated)
Updated on ClinicalTrials.gov 2026-08-11