Track this trial free. DataLookout checks ClinicalTrials.gov daily and emails you which fields changed on NCT07633951 (status, enrollment, completion dates, endpoints, sites) when this record is updated. Free accounts track up to 5 trials.

Track this trial

Multicenter Epidemiological Study for the Evaluation of the Seroprevalence of Total and Neutralizing Antibodies Against Adenoassociated Virus Serotypes Used in Gene Therapy in Patients With Neuromuscular Diseases of Genetic Origin.

Study acronym: SeroDysMyo
StatusNot Yet Recruiting
PhaseNot applicable
SponsorGenethon
Started
View on ClinicalTrials.gov ↗

Record History

  1. Minor Study First Submitted
9 trials monitored
See all monitored trials
This study aims to assess the overall seroprevalence of neutralizing antibodies against different AAVs potentially used in gene therapy in patients with genetic neuromuscular diseases.
Trial Details
NCT Number NCT07633951
Lead Sponsor Genethon
Conditions
(from sponsor)
Neuromuscular Deficits, Genetic Disorder
Related terms Genetic Diseases, Inborn
Enrollment 450 participants
Start Date
Primary Completion (estimated)
Study Completion (estimated)
Updated on ClinicalTrials.gov