Sponsor Pipeline

Genethon Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-08-16
5
Active Trials
3
Recruiting
1
Disease Areas
Active Trials by Phase
Phase 2
1
Phase 1/2
1
Not specified
3
Active Trials
NCT IDTitleConditionStatus
Phase 2
NCT06518005 Efficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe… Crigler-Najjar Syndrome Recruiting
Phase 1/2
NCT02333760 Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott… Wiskott-Aldrich Syndrome Active, Not Recruiting
Not specified
NCT03466463 Gene Therapy for Severe Crigler Najjar Syndrome Crigler-Najjar Syndrome Recruiting
NCT03882827 Natural History of Duchenne Muscular Dystrophy Duchenne Muscular Dystrophy Recruiting
NCT07633951 Multicenter Epidemiological Study for the Evaluation of the Seroprevalence of Total and… Neuromuscular Deficits Not Yet Recruiting
Disease Areas
Duchenne Muscular Dystrophy (1)
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