Clinical Trial

Expanded Access Program of Bitopertin For Participants With EPP or XLP

Name: Expanded Access Program of Bitopertin For Participants With EPP or XLP — clinical trial record (NCT07603401)
Creator: DataLookout
License: https://creativecommons.org/licenses/by/4.0/

Available

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Summary

The goal of this expanded access program is to provide bitopertin to patients with EPP and XLP who have no satisfactory treatment options available in the US and to learn if bitopertin is safe to treat EPP and XLP.

Protocol Amendment History 1 change

critical Trial status changed: Temporarily Not Available → Available 2026-06-17

Trial Details

NCT Number	NCT07603401
Lead Sponsor	Disc Medicine, Inc
Conditions	Erythropoietic Protoporphyria (EPP), X-Linked Protoporphyria (XLP)
Updated on ClinicalTrials.gov	2026-08-03