Clinical Trial

BAG3-DCM Natural History Study

Not Yet Recruiting
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Summary
The goal of this international observational study is to learn about the natural history of Dilated Cardiomyopathy (DCM) arising from pathogenic BAG3 variants in adult patients ≥18 years of age.
Trial Details
NCT Number NCT07486752
Lead Sponsor Rocket Pharmaceuticals Inc.
Conditions Dilated Cardiomyopathy (DCM), Cardiovascular Diseases, Heart Diseases, Genetic Diseases
Enrollment 30 participants
Start Date 2026-05
Primary Completion 2032-12 (estimated)
Study Completion 2033-03 (estimated)
Updated on ClinicalTrials.gov 2026-03-20