| NCT Number | NCT07314736 |
| Lead Sponsor | St. Jude Children's Research Hospital |
| Conditions | Rare Disorder, Disorder, Neurologic |
| Enrollment | 385 participants |
| Start Date | 2026-07-08 |
| Primary Completion | 2031-01 (estimated) |
| Study Completion | 2031-01 (estimated) |
| Updated on ClinicalTrials.gov | 2026-07-13 |