| NCT Number | NCT07206095 |
| Lead Sponsor | Hospital Universitari Vall d'Hebron Research Institute
Collaborators: Hospital Clinic of Barcelona, Institute for Bioengineering of Catalonia, Hospital Arnau de Vilanova, Lleida (Spain) |
| Conditions | Sickle Cell Disease, Thalassaemia, Congenital Dyserythropoietic Anemia (CDA), Enzyme Disorder; Anemia, Spherocytosis, Hereditary, Stomatocytosis, Hemoglobin Disorder, Anemia Due to Membrane Defect +1 more |
| Enrollment | 200 participants |
| Start Date | 2020-11-13 |
| Primary Completion | 2025-05-25 (estimated) |
| Study Completion | 2028-05 (estimated) |
| Updated on ClinicalTrials.gov | 2025-10-03 |