The purpose of this study is to provide participants who successfully completed the study titled "An Open-label, Safety Study for Previously Treated Vatiquinone (PTC743) Subjects With Inherited Mitochondrial Disease" with liquid Vatiquinone through an intermediate patient population expanded access protocol.
Protocol Amendment History
1 amendment
This ClinicalTrials.gov record has been amended once since 2025-09-04.
Status change: Available → No Longer Available2026-04-03