Clinical Trial

A Study of Patients With Fabry Disease (US Specific)

Recruiting
View on ClinicalTrials.gov →
Summary
This is an observational study to evaluate the effects of treatment on long-term effectiveness, safety, and health-related quality of life (HRQOL) in patients with Fabry disease, with a main focus on migalastat.
Protocol Amendment History 12 amendments
This ClinicalTrials.gov record has been amended 12 times since 2025-03-26; most recent amendment 2026-07-09.
Status change: Not Yet Recruiting → Recruiting 2026-01-13
Trial Details
NCT Number NCT06906367
Lead Sponsor Amicus Therapeutics
Conditions Fabry Disease
Enrollment 450 participants
Start Date 2026-02-13
Primary Completion 2032-06 (estimated)
Study Completion 2032-06 (estimated)
Updated on ClinicalTrials.gov 2026-07-10