| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 3 | |||
| NCT04808505 | A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase… | Glycogen Storage Disease Type II Infantile Onset | Recruiting |
| NCT06904261 | A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and… | Fabry Disease | Recruiting |
| NCT03911505 | ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in… | Pompe Disease (Late-onset) | Active, Not Recruiting |
| NCT04020055 | A Study to Evaluate Migalastat in Fabry Subjects With Amenable GLA Variant and Renal… | Fabry Disease | Active, Not Recruiting |
| Not specified | |||
| NCT04252066 | A Global Prospective Observational Study of Women With Fabry Disease and Their Infants… | Fabry Disease | Recruiting |
| NCT06121011 | A Global Prospective Observational Registry of Patients With Pompe Disease | Pompe Disease | Recruiting |
| NCT06906367 | A Study of Patients With Fabry Disease (US Specific) | Fabry Disease | Recruiting |