Clinical Trial

PKP2-ACM Natural History Study

Recruiting
View on ClinicalTrials.gov →
Summary
The goal of this study is to describe the natural history and clinical events for patients who have Arrhythmogenic Cardiomyopathy with Pathogenic Plakophilin-2 Variants (PKP2-ACM) managed with standard of care.
Protocol Amendment History 5 amendments
This ClinicalTrials.gov record has been amended 5 times since 2024-10-14; most recent amendment 2026-02-24.
Status change: Not Yet Recruiting → Recruiting 2025-09-16
Trial Details
NCT Number NCT06644742
Lead Sponsor Rocket Pharmaceuticals Inc.
Conditions Cardiomyopathies, Heart Diseases, Cardiovascular Diseases, Genetic Diseases
Enrollment 36 participants
Start Date 2026-03
Primary Completion 2030-12 (estimated)
Study Completion 2031-04 (estimated)
Updated on ClinicalTrials.gov 2026-02-27