Clinical Trial

Danon Disease Natural History Study

Name: Danon Disease Natural History Study — clinical trial record (NCT06214507)
Creator: DataLookout
License: https://creativecommons.org/licenses/by/4.0/

Recruiting

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Summary

The goal of this international observational study is to learn about the natural history of Danon disease in male patients (≥8 years of age) and female patients (8 to 50 years of age).

Protocol Amendment History 12 amendments

This ClinicalTrials.gov record has been amended 12 times since 2024-01-10; most recent amendment 2026-07-27.

Trial Details

NCT Number	NCT06214507
Lead Sponsor	Rocket Pharmaceuticals Inc.
Conditions	Danon Disease
Enrollment	60 participants
Start Date	2023-12-20
Primary Completion	2029-12 (estimated)
Study Completion	2030-03 (estimated)
Updated on ClinicalTrials.gov	2026-07-28