Clinical Trial

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

Recruiting
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Summary
This is a global prospective observational study of women with Fabry disease and their infants during pregnancy and/or breastfeeding. The study will evaluate outcomes of pregnancy and/or breastfeeding in women and infants exposed to migalastat.
Protocol Amendment History 6 amendments
This ClinicalTrials.gov record has been amended 6 times since 2020-01-30; most recent amendment 2025-07-02.
Status change: Not Yet Recruiting → Recruiting 2020-04-27
Trial Details
NCT Number NCT04252066
Lead Sponsor Amicus Therapeutics
Conditions Fabry Disease
Enrollment 20 participants
Start Date 2025-03-18
Primary Completion 2029-08 (estimated)
Study Completion 2030-02 (estimated)
Updated on ClinicalTrials.gov 2025-07-08