Clinical Trial

Natural History of Duchenne Muscular Dystrophy

Recruiting
View on ClinicalTrials.gov →
Summary
Baseline Study on Duchenne Muscular Dystrophy (DMD) in view to collect data on the natural disease course in a cohort in young male subjects aged from 4 to 9 Years over a period of 6 to 36 months using disease appropriate evaluations.
Protocol Amendment History 11 amendments
This ClinicalTrials.gov record has been amended 11 times since 2019-03-19; most recent amendment 2026-02-10.
Status change: Not Yet Recruiting → Recruiting 2020-01-06
Trial Details
NCT Number NCT03882827
Lead Sponsor Genethon
Conditions Duchenne Muscular Dystrophy
Enrollment 220 participants
Start Date 2019-12-19
Primary Completion 2029-05-30 (estimated)
Study Completion 2029-09-30 (estimated)
Updated on ClinicalTrials.gov 2026-02-12