| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 3 | |||
| NCT07503444 | A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome | Rett Syndrome | Not Yet Recruiting |
| NCT06118255 | A Study to Evaluate Safety, Tolerability, and Pharmacokinetics of Fenfluramine… | Dravet Syndrome | Active, Not Recruiting |
| Phase 2 | |||
| NCT03845712 | An Open-Label Study of Continuation Treatment With Combination Pyrimidine Nucleosides in… | Thymidine Kinase 2 Deficiency | Active, Not Recruiting |