| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 1/2 | |||
| NCT07102524 | Intrathecal Gene Therapy For SLC13A5 Citrate Transporter Disorder | SLC13A5 Citrate Transporter Disorder | Recruiting |
| Not specified | |||
| NCT04681781 | SLC13A5 Deficiency Natural History Study - Remote Only | Citrate Transporter Deficiency | Enrolling by Invitation |
| NCT06144957 | SLC13A5 Deficiency Natural History Study - United States Only | Citrate Transporter Deficiency | Enrolling by Invitation |